Rare Diseases Rare disease medicines and hard-to-source specialty brands move through Appleglc.com to support hospitals, doctors, patients, and tenders using regulated access pathways and resilient global supply networks. Home 5 Rare Diseases Neurodevelopmental & Epilepsy Movement Disorders Spinal Muscular Atrophy Muscular Dystrophy & Myopathy Motor Neuron Disease & NMJ Ataxias & Spastic Paraplegia Tuberous Sclerosis & Phakomatoses Lysosomal Storage Disorders Amino Acid & Urea Cycle Mitochondrial Disorders Copper / Iron / Mineral Lipid & Lipodystrophy Glycogen Storage Cystic Fibrosis & Pulmonary Cardiomyopathy & Cardiac Amyloid Connective Tissue / Vascular HAE & Complement Disorders Hemoglobinopathy Hemophilia & Bleeding Bone Marrow Failure & Anemia Myeloproliferative & Mastocytosis Rare Leukemias Rare Lymphomas Multiple Myeloma Targeted Fusion Cancers Rare GI / HPB Cancers & NETs Rare Endocrine Cancers Rare GU & Gyn Cancers GIST & Soft Tissue Sarcoma Pediatric Solid Tumors CNS Tumors & Mesothelioma Hereditary Cancer Syndromes & NF Primary Immunodeficiency Autoinflammatory & Behçet Vasculitis & Connective Tissue Disease Eosinophilic Diseases GVHD Cholestatic & Liver Disease Rare GI Disorders Renal & Glomerular Skeletal Dysplasia & Bone Pituitary, GH & DI Adrenal & Cortisol Parathyroid & Calcium Sex Chromosome & Reproductive Genetic Obesity / Leptin / Wolfram Inherited Retinal Disease Porphyria Inflammatory Skin & Blistering Demyelinating & Other Neuro Pancreatic Enzyme Insufficiency Rare Infectious Diseases (Biothreat / NTM) Refractory Migraine / Cluster Headache CTEPH (Chronic Thromboembolic PH)
